• New Investigational Drug

    We are currently researching a new investigational drug to see if it may help preserve or improve muscle function in Duchenne muscular dystrophy (DMD). We are looking for boys who are 6 to 15 years old with DMD to participate in a clinical research trial to examine the safety and effectiveness of this new investigational drug.

  • Clinical Research Trial

    Prior to making a new drug available to doctors or their patients, drug companies must test the investigational drug in a series of clinical research trials. The safety and tolerability of this current investigational drug for DMD have already been demonstrated in healthy adult subjects in a previous clinical trial.  The next step is to study the safety and effectiveness of this investigational drug in boys with DMD.  If your son has been diagnosed with DMD and is 6 to 15 years old, he may be eligible to participate in this clinical trial.